Several Techniques Have Been Developed to Treat Blood Disorders Caused

Several techniques have been developed to treat blood disorders caused by genetic mutations.  Which of the following methods would be most effective in the treatment of a patient homozygous for a deleterious mutation in a gene coding for a subunit of hemoglobin?

A) Replacement of the mutant gene with a functional copy in red blood cells
B) Treatment with a drug that increases red blood cell production
C) Introduction and activation of a functional hemoglobin gene in bone marrow stem cells
D) Single blood transfusion from a patient homozygous for the wild-type hemoglobin gene

Correct Answer:

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